Company profile

SpliceBio

Cell & gene therapyChallengingFounded 2019

Protein-splicing gene therapy — SB-007, the first dual-AAV gene therapy cleared by the FDA for Stargardt disease.

About

Protein-splicing platform (split-intein AAV) to deliver large genes. Lead program SB-007 for Stargardt (ABCA4) in Phase 1/2 (ASTRA study), backed by EQT Life Sciences and Sanofi Ventures.

HQ: Barcelona, Spain

Funding

$135M Series B (Jun 2025)