Company profile

Atsena Therapeutics

Cell & gene therapyChallengingFounded 2019

Ocular AAV gene therapy — ATSN-101 for LCA1 (Lancet-published Phase 1/2 data) heading to a pivotal Phase 3.

About

Ocular AAV gene therapy company. Lead programs ATSN-101 for GUCY2D-associated LCA1 (12-month Phase 1/2 data published in The Lancet, Sep 2024) and ATSN-201 for X-linked retinoschisis. RMAT designation held.

HQ: Durham, NC, USA

Funding

$150M Series C (Apr 2025, Bain Capital Life Sciences-led)
Total raised ~$175M–$238M depending on source.